RARECast

548 Episoder

1. Accelerating the Development of Genetic Medicines with AI

   Publisert: 7.12.2023
2. Leveraging AI to Address the Neuropsychiatric Conditions Associated with a Rare Disease

   Publisert: 30.11.2023
3. In Pursuit of a Treatment for His Son, A Lawyer Becomes a Biotech Executive

   Publisert: 22.11.2023
4. In Push for Treatment, a Patient Organization Becomes a Trial Sponsor

   Publisert: 16.11.2023
5. Delayed Diagnosis of Rare Diseases Takes Staggering Economic Toll

   Publisert: 9.11.2023
6. A Cell Therapy to Control Heart-Damaging Inflammation in Duchenne

   Publisert: 2.11.2023
7. Stimulating the Growth of Muscle Mass in People with Neuromuscular Diseases

   Publisert: 26.10.2023
8. Turning Grief into Action

   Publisert: 19.10.2023
9. A Plea to the FDA to Give an Ultra-Rare Disease Drug a Fair Hearing

   Publisert: 12.10.2023
10. How the Woolly Mammoth Beat a Path to Better Gene Therapies

    Publisert: 5.10.2023
11. A Genetic Counselor’s Journey into Patient Advocacy

    Publisert: 28.9.2023
12. A Company in the Fold of Rare Disease

    Publisert: 21.9.2023
13. Disabling Antibodies that Drive Rare, Immunological Conditions

    Publisert: 14.9.2023
14. Keeping the Sentinels of the Brain Vigilant

    Publisert: 7.9.2023
15. Considering the Unfinished Work in Cystic Fibrosis

    Publisert: 31.8.2023
16. How to Advocate for Yourself as You Battle Cancer

    Publisert: 24.8.2023
17. Targeting Neuroinflammation to Treat ALS

    Publisert: 17.8.2023
18. Leveraging Community Partnerships to Address a Rare Disease Behind a Medical Mystery in New Mexico

    Publisert: 10.8.2023
19. Accelerating Gene Editing Therapies for Rare, Neurological Conditions

    Publisert: 3.8.2023
20. Inhibiting Electrical Activity in Rare, Seizure Disorders

    Publisert: 27.7.2023