RARECast

548 Episoder

1. Part 4-Gene Therapy: A Researcher’s Perspective

   Publisert: 13.11.2020
2. Part 3-Gene Therapy: An Industry Perspective

   Publisert: 6.11.2020
3. Part 2-Gene Therapy: A Patient Advocate's Perspective

   Publisert: 29.10.2020
4. Part 1-Gene Therapy: A Genetic Counselor’s Perspective

   Publisert: 23.10.2020
5. An App to Make Patients the Experts in their Own Conditions

   Publisert: 15.10.2020
6. Pursuing a New Target for Autoimmune Diseases

   Publisert: 8.10.2020
7. Finding a Rare Friend

   Publisert: 2.10.2020
8. Industrializing Individual Therapies for People with Rare Conditions

   Publisert: 25.9.2020
9. Rare Disease Advocate Turned Filmmaker Turns Lens on his Son

   Publisert: 17.9.2020
10. Inhibiting Signaling that Drives Growth of Rare Malformations

    Publisert: 10.9.2020
11. Readying a Rare Disease Community for the Availability of Treatments

    Publisert: 3.9.2020
12. Forging a Rare Disease Research Agenda

    Publisert: 27.8.2020
13. Delivering Injectable Drugs Orally

    Publisert: 20.8.2020
14. What Young Adults with Rare Conditions Need to Know About Health Insurance

    Publisert: 14.8.2020
15. Mirum Prepares to Seek Approval for Rare Liver Disease Therapy

    Publisert: 7.8.2020
16. Payer Perceptions of Fairness in Pricing Rare Disease Therapies

    Publisert: 4.8.2020
17. Improving Narcolepsy Therapy with Drug Delivery Technology

    Publisert: 23.7.2020
18. Fighting the Persistent Cough in a Rare and Deadly Lung Disease

    Publisert: 15.7.2020
19. Targeting Huntington's Disease with Antisense

    Publisert: 8.7.2020
20. Assembling a Pipeline for Rare GI Disorders

    Publisert: 1.7.2020